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Cure Rare Disease

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BiotecnologíaCienciaFarmacéuticaSaludVoluntariado/Solidaridad/ONGs
24/09/2025
Voluntariado/Solidaridad/ONGs
Industria
Salud
Higiene alimentaria
Biotecnología
Medicina - Varios
Farmacéutica
Cure Rare Disease Secures FDA Orphan Drug Designation for Investigational Gene Therapy to Treat Limb-Girdle Muscular Dystrophy Type R9 (LGMD2i/R9)
1.00
24/06/2025
Ciencia
Higiene alimentaria
Biotecnología
Salud
Farmacéutica
Sanidad
Voluntariado/Solidaridad/ONGs
Industria
Cure Rare Disease Receives FDA Feedback on Limb-Girdle 2i/R9 Gene Therapy Program Following Successful Pre-IND Meeting
1.00
23/06/2025
Ciencia
Higiene alimentaria
Biotecnología
Salud
Farmacéutica
Sanidad
Voluntariado/Solidaridad/ONGs
Industria
Cure Rare Disease Receives FDA Feedback on Limb-Girdle 2i/R9 Gene Therapy Program Following Successful Pre-IND Meeting
1.00
09/06/2025
Ciencia
Biotecnología
Farmacéutica
Sanidad
Salud
Voluntariado/Solidaridad/ONGs
Mercado laboral
Cure Rare Disease Welcomes New Scientific and Strategic Leaders to Advance Therapies for Ultra-Rare Conditions
1.00
14/05/2025
Voluntariado/Solidaridad/ONGs
Industria
Ciencia
Biotecnología
Farmacéutica
Salud
Higiene alimentaria
Medicina - Varios
Cure Rare Disease Receives Orphan Drug Designation from FDA for Investigational Therapy Targeting Spinocerebellar Ataxia Type 3 (SCA3)
1.00
03/04/2025
Multimedia
Voluntariado/Solidaridad/ONGs
Eventos
Biotecnología
Deportes
Salud
Familia
Ir de compras
Asociaciones/Profesionales
Ciencia
Infancia
We Row For William: 157 Miles, One Nonstop Journey of Hope
1.00
06/02/2025
Biotecnología
Salud
Ciencia
Voluntariado/Solidaridad/ONGs
Cure Rare Disease Awarded $5.69 Million CIRM Grant to Advance Gene Therapy for Spinocerebellar Ataxia Type 3
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