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Genethon

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BiotecnologiaFarmaceuticaIndustriaMedicina - VarieSalute
10/10/2025
Multimedialità
Scienza
Biotecnologia
Farmaceutica
Sanità
Salute
Medicina - Varie
Eventi
Fiere
Industria
Data from GNT-018-IDES Trial Supports Feasibility of imlifidase as Pretreatment in Gene Therapy Treatment for Patients With Crigler–Najjar Syndrome Who Are Immune to AAV
1.00
09/10/2025
Scienza
Biotecnologia
Farmaceutica
Sanità
Salute
Medicina - Varie
Web e Social Network
Volontariato/Solidarietà/Non profit
Eventi
Industria
Genethon Confirms 2-Year Efficacy in Duchenne Muscular Dystrophy Patients Treated With Its Low Dose Micro-Dystrophin Gene Therapy (GNT0004) at the ESGCT 32nd Annual Congress
1.00
28/07/2025
Industria
Biotecnologia
Salute
Farmaceutica
Medicina - Varie
Genethon to Launch Pivotal Trial in Europe of GNT0004 a Low-Dose Microdystrophin Gene Therapy for Duchenne Muscular Dystrophy
1.00
27/02/2025
Salute
HIV, AIDS e malattie autoimmuni
Biotecnologia
Medicina - Varie
Farmaceutica
Industria
Genethon Celebrates Rare Disease Day by Highlighting New Technologies to Advance Gene Therapies and Bring Hope to Millions of Patients Worldwide
1.00
19/12/2024
Tecnica
Scienza
Biotecnologia
Medicina - Varie
Salute
Farmaceutica
Volontariato/Solidarietà/Non profit
Industria
A Phase 3 Ready DMD Gene Therapy, a Clinical Trial to Offset AAV Neutralizing Antibodies, and an AI Inspired New Generation of Capsids Highlight Genethon’s 2024 Fall Milestones
1.00
03/12/2024
Multimedialità
Industria
Salute
Biotecnologia
Medicina - Varie
Scienza
Farmaceutica
Genethon and Hansa Biopharma Announce Initiation of a Phase 2 Trial of imlifidase as a Pre-Treatment to GNT-0003 in Severe Crigler-Najjar Syndrome
1.00
21/10/2024
Eventi
Fiere
Industria
Tecnica
HIV, AIDS e malattie autoimmuni
Sanità
Famiglia
Biotecnologia
Vetrine/Shopping
Medicina - Varie
Cardiologia
Salute
Giovani
Terza età
Infanzia
Genethon to Showcase the Latest Advances in Gene Therapies for Multiple Diseases at the ESGCT 31st Annual Congress October 22 – 25, 2024 in Rome, Italy
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